Handbook_Volume III

126 1. Aspetti Generali Bibliografia 1. Snowden JA, Sánchez-Ortega I, Corbacioglu S, Basak GW, Chabannon C, de la Camara R, et al. Indications for haematopoietic cell transplantation for haematological diseases, solid tumours and immune disorders: current practice in Europe, 2022. Bone Marrow Transplant 2022 [Internet]. 2022 May 19 [cited 2022 Jun 21];1–23. Available from: https://www.nature.com/articles/s41409022-01691-w 2. Niederwieser D, Baldomero H, Bazuaye N, Bupp C, Chaudhri N, Corbacioglu S, et al. One and a half million hematopoietic stem cell transplants: continuous and differential improvement in worldwide access with the use of non-identical family donors. Haematologica [Internet]. 2022 May 1 [cited 2022 Jun 23];107(5):1045– 53. Available from: https://pubmed.ncbi.nlm.nih.gov/34382386/ 3. Passweg JR, Baldomero H, Chabannon C, Basak GW, de la Cámara R, Corbacioglu S, et al. Hematopoietic cell transplantation and cellular therapy survey of the EBMT: monitoring of activities and trends over 30 years. Bone Marrow Transplant [Internet]. 2021 Jul 1 [cited 2022 Jun 23];56(7):1651–64. Available from: https://pubmed.ncbi.nlm.nih.gov/33623153/ 4. Hematopoietic stem cell transplantation in childhood: report from the bone marrow transplantation group of the Associazione Italiana Ematologia Oncologia Pediatrica (AIEOP) | Haematologica [Internet]. [cited 2022 Jun 29]. Available from: https://www. haematologica.org/article/view/1712 5. Majhail NS, Brazauskas R, Hassebroek A, Bredeson CN, Hahn T, Hale GA, et al. Outcomes of allogeneic hematopoietic cell transplantation for adolescent and young adults compared with children and older adults with acute myeloid leukemia. Biol Blood Marrow Transplant [Internet]. 2012 Jun [cited 2022 May 23];18(6):861–73. Available from: https://pubmed.ncbi.nlm.nih. gov/22040843/ 6. Wood WA, Lee SJ, Brazauskas R, Wang Z, Aljurf MD, Ballen KK, et al. Survival improvements in adolescents and young adults after myeloablative allogeneic transplantation for acute lymphoblastic leukemia. Biol Blood Marrow Transplant [Internet]. 2014 [cited 2022 May 23];20(6):829–36. Available from: https://pubmed.ncbi.nlm.nih.gov/24607554/ 7. MacMillan ML, Wagner JE. Haematopoeitic cell transplantation for Fanconi anaemia – when and how? Br J Haematol [Internet]. 2010 Apr 1 [cited 2022 Jun 29];149(1):14–21. Available from: https:// onlinelibrary.wiley.com/doi/full/10.1111/j.1365-2141.2010.08078.x 8. Bartelink IH, Lalmohamed A, van Reij EML, Dvorak CC, Savic RM, Zwaveling J, et al. Association of busulfan exposure with survival and toxicity after haemopoietic cell transplantation in children and young adults: a multicentre, retrospective cohort analysis. Lancet Haematol [Internet]. 2016 Nov 1 [cited 2022 Jun 14];3(11):e526–36. Available from: https://pubmed.ncbi.nlm.nih. gov/27746112/ 9. Bartelink IH, Boelens JJ, Bredius RGM, Egberts ACG, Wang C, Bierings MB, et al. Body weight-dependent pharmacokinetics of busulfan in paediatric haematopoietic stem cell transplantation patients: towards individualized dosing. Clin Pharmacokinet [Internet]. 2012 [cited 2022 Jun 14];51(5):331–45. Available from: https://pubmed.ncbi.nlm.nih.gov/22455797/ 10. Admiraal R, Nierkens S, Bierings MB, Bredius RGM, van Vliet I, Jiang Y, et al. Individualised dosing of anti-thymocyte globulin in paediatric unrelated allogeneic haematopoietic stem-cell transplantation (PARACHUTE): a single-arm, phase 2 clinical trial. Lancet Haematol [Internet]. 2022 Feb 1 [cited 2022 Jun 14];9(2):e111–20. Available from: http://www.thelancet.com/article/ S2352302621003756/fulltext 11. Chiesa R, Standing JF, Winter R, Nademi Z, Chu J, Pinner D, et al. Proposed Therapeutic Range of Treosulfan in Reduced Toxicity Pediatric Allogeneic Hematopoietic Stem Cell Transplant Conditioning: Results From a Prospective Trial. Clin Pharmacol Ther [Internet]. 2020 Aug 1 [cited 2022 Jun 14];108(2):264–73. Available from: https://pubmed.ncbi.nlm.nih.gov/31701524/ 12. Schrezenmeier H, Passweg JR, Marsh JCW, Bacigalupo A, Bredeson CN, Bullorsky E, et al. Worse outcome and more chronic GVHD with peripheral blood progenitor cells than bone marrow in HLA-matched sibling donor transplants for young patients with severe acquired aplastic anemia. Blood [Internet]. 2007 Aug 15 [cited 2022 Jun 16];110(4):1397–400. Available from: https://pubmed.ncbi.nlm.nih.gov/17475907/ 13. Eapen M, Le Rademacher J, Antin JH, Champlin RE, Carreras J, Fay J, et al. Effect of stem cell source on outcomes after unrelated donor transplantation in severe aplastic anemia. Blood [Internet]. 2011 Sep 1 [cited 2022 Jun 16];118(9):2618–21. Available from: https://pubmed.ncbi.nlm.nih.gov/21677312/ 14. Eapen M, Horowitz MM, Klein JP, Champlin RE, Loberiza FR, Ringdén O, et al. Higher mortality after allogeneic peripheral-blood transplantation compared with bone marrow in children and adolescents: the Histocompatibility and Alternate Stem Cell Source Working Committee of the International Bone Marrow Transplant Registry. J Clin Oncol [Internet]. 2004 Dec 15 [cited 2022 Jun 16];22(24):4872–80. Available from: https://pubmed. ncbi.nlm.nih.gov/15520055/ 15. Simonin M, Dalissier A, Labopin M, Willasch A, Zecca M, Mouhab A, et al. More chronic GvHD and non-relapse mortality after peripheral blood stem cell compared with bone marrow in hematopoietic transplantation for paediatric acute lymphoblastic leukemia: a retrospective study on behalf of the EBMT Paediatric Diseases Working Party. Bone Marrow Transplant [Internet]. 2017 Jul 1 [cited 2022 Jun 16];52(7):1071–3. Available from: https://pubmed.ncbi.nlm.nih.gov/28394370/ 16. Heimall J, Logan BR, Cowan MJ, Notarangelo LD, Griffith LM, Puck JM, et al. Immune reconstitution and survival of 100 SCID patients post–hematopoietic cell transplant: a PIDTC natural history study. Blood [Internet]. 2017 Dec 21 [cited 2022 Jun 16];130(25):2718–27. Available from: https://ashpublications.org/ blood/article/130/25/2718/36871/Immune-reconstitution-and-survival-of-100-SCID 17. Eapen M. A resurgence of cord blood transplantation? Lancet Haematol [Internet]. 2020 Feb 1 [cited 2022 Jun 29];7(2):e89–90. Available from: http://www.thelancet.com/article/ S2352302619302340/fulltext 18. Ruggeri A, Volt F, Locatelli F, Michel G, Diaz de Heredia C, Abecasis M, et al. Unrelated Cord Blood Transplantation for Acute Leukemia Diagnosed in the First Year of Life: Outcomes and Risk Factor Analysis. Biol Blood Marrow Transplant [Internet]. 2017 Jan 1 [cited 2022 Jun 16];23(1):96–102. Available from: http://www. astctjournal.org/article/S1083879116304281/fulltext 19. Rocha V, Cornish J, Sievers EL, Filipovich A, Locatelli F, Peters C, et al. Comparison of outcomes of unrelated bone marrow and umbilical cord blood transplants in children with acute leukemia. Blood [Internet]. 2001 May 15 [cited 2022 Jun 19];97(10):2962–71. Available from: https://ashpublications.org/